#muscular dystrophy — top 20, last 30d
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Xylose phosphatase activity of dystroglycan self-regulates its receptor function.
(science.org)
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Science 2026-08-13 | #glycosylation #extracellular matrix #phosphatase #dystroglycan #muscular dystrophy | |
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An antisense method for efficient exon skipping and its application to Duchenne muscular dystrophy.
(pnas.org)
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PNAS 2026-08-10 | #antisense #exon skipping #muscular dystrophy #splicing #therapeutics | |
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TRF2 couples muscle stem cell identity to regenerative repair.
(science.org)
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Science Advances 2026-07-31 | #regeneration #stem cell #muscular dystrophy #myogenesis #transcription | |
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Deramiocel heart-derived cellular therapy in advanced Duchenne muscular dystrophy (HOPE-3): a phase 3, randomised, double-blind, placebo-controlled trial.
(linkinghub.elsevier.com)
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The Lancet 2026-07-29 | #muscular dystrophy #clinical trial #cell therapy #cardiomyopathy |