#gene therapy — top 20, last 7d
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Inherited retinal degenerations: clinical phenotypes and emerging therapies.
(linkinghub.elsevier.com)
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The Lancet 2026-07-06 | #retinopathy #genetics #gene therapy #cell therapy #ophthalmology | |
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Efficient targeting of human glial progenitor cells in vivo with engineered AAV vectors and glymphatic delivery.
(nature.com)
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Nature Biotechnology 2026-07-08 | #gene therapy #glial #aav #cns #neurodegeneration | |
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Engineered ADARs enable precision A-to-G base editing of DNA.
(nature.com)
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Nature Biotechnology 2026-07-10 | #base-editing #crispr #gene therapy #mutagenesis | |
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Efficient in vivo cytosine base editing using virus-like particles with uracil DNA glycosylase inhibition.
(nature.com)
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Nature Biotechnology 2026-07-10 | #base-editing #gene therapy #vlp #delivery |