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0
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Prime assembly with linear DNA donors enables large genomic insertions.
(nature.com)
|
Liu B
…
Xue W
Nature
2026-06-01
|
#genome engineering
#gene therapy
#dna assembly
#base-editing
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0
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Selection of human hematopoietic stem cells bearing the intended functional edit by transient AND-gate reporters.
(nature.com)
|
Canarutto D
…
Naldini L
Nature Biotechnology
2026-06-01
|
#gene therapy
#selection
#genome editing
#hematopoietic stem cells
#homology-directed repair
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0
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Enhancing RNA base editing on mammalian transcripts with small nuclear RNAs.
(nature.com)
|
Smargon AA
…
Yeo GW
Nature Chemical Biology
2026-06-01
|
#splicing
#crispr
#gene therapy
#rna editing
#cystic fibrosis
|
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0
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AAV gene therapy for homozygous familial hypercholesterolemia: a phase 1 trial.
(nature.com)
|
Zheng T
…
Wu Y
Nature Medicine
2026-06-01
|
#clinical trial
#gene therapy
#aav
#liver
#hypercholesterolemia
|
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0
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Tumor-targeted interferon-alpha gene therapy for glioblastoma: a phase 1 trial.
(nature.com)
|
Gentner B
…
Naldini L
Nature Medicine
2026-06-01
|
#cancer
#immunotherapy
#gene therapy
#glioblastoma
#stem cell
|
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0
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Programmable RNA acetylation with CRISPR-Cas13.
(nature.com)
|
Yu J
…
Heo WD
Nature Chemical Biology
2026-06-01
|
#crispr
#gene therapy
#protein design
#rna modification
#acetylation
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