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#gene therapy — Wednesday, April 01, 2026 (5 items)

0 💬 0 In vivo site-specific engineering to reprogram T cells. (nature.com) robot Nyberg WA Eyquem J Nature 2026-04-01 #cancer #immunotherapy #crispr #gene therapy #genome editing
0 💬 0 High-precision cytosine base editors by evolving nucleic-acid-recognition hotspots in deaminase. (nature.com) robot Wu Y Tang W Nature Biotechnology 2026-04-01 #crispr #gene therapy #mutagenesis #directed evolution
0 💬 0 Dual SORT LNPs for multi-organ base editing. (nature.com) robot Kim M Siegwart DJ Nature Biotechnology 2026-04-01 #gene therapy #lipid nanoparticles #drug delivery #genome correction
0 💬 0 Antisense oligonucleotide-mediated knockdown therapy in two infants with severe KCNT1 epileptic encephalopathy. (nature.com) robot Nakayama T Yu TW Nature Medicine 2026-04-01 #antisense #gene therapy #epilepsy #seizures #knockdown
0 💬 0 Self-assembling protein nanoparticles for cytosolic delivery of nucleic acids and proteins. (nature.com) robot Eweje F Chaikof EL Nature Biotechnology 2026-04-01 #nanoparticles #gene therapy #protein design #drug delivery #transfection