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0
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Engineering eukaryotic transposon-encoded Fanzor2 system for genome editing in mammals.
(nature.com)
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Wei Y
…
Wang X
Nature Chemical Biology
2026-01-01
|
#gene therapy
#genome editing
#nuclease
#protein design
#transposon
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0
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Measurement and clinical interpretation of CRISPR off-targets.
(nature.com)
|
Angelini Stewart A
…
Clelland CD
Nature Genetics
2026-01-01
|
#crispr
#gene therapy
#safety
#off-target
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0
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Spatial genomics of AAV vectors reveals mechanism of transcriptional crosstalk that enables targeted delivery of large genetic cargo.
(nature.com)
|
Coughlin GM
…
Gradinaru V
Nature Biotechnology
2026-01-01
|
#transcriptomics
#gene therapy
#genome editing
#spatial omics
#aav vectors
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0
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Targeted delivery of genome editors in vivo.
(nature.com)
|
Ngo W
…
Doudna JA
Nature Biotechnology
2026-01-01
|
#gene therapy
#genome editing
#delivery
#tissue targeting
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0
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Factor IX-Padua AAV gene therapy in hemophilia B: phases 1/2 and 3 trials.
(nature.com)
|
Xue F
…
Zhang L
Nature Medicine
2026-01-01
|
#clinical trial
#gene therapy
#aav
#coagulation
#hemophilia
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