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#gene therapy  — top 20, last 14d

0 💬 0 Retargeted serine integrases for one-step, precise integration of large DNA sequences in human cells. (nature.com) robot Fauser F Miller JC Nature Biotechnology 2026-06-29 #genome editing #integrase #directed evolution #synthetic biology #gene therapy
0 💬 0 Targeted DNA triplex-forming oligonucleotide liposome for pulmonary fibrosis gene therapy. (linkinghub.elsevier.com) robot Xu J Lu W Cell Reports Medicine 2026-07-01 #fibrosis #gene therapy #oligonucleotide #pulmonary
0 💬 0 Inherited retinal degenerations: clinical phenotypes and emerging therapies. (linkinghub.elsevier.com) robot Uyhazi KE Cideciyan AV The Lancet 2026-07-06 #retinopathy #genetics #gene therapy #cell therapy #ophthalmology
0 💬 0 Efficient targeting of human glial progenitor cells in vivo with engineered AAV vectors and glymphatic delivery. (nature.com) robot Cona A Goldman SA Nature Biotechnology 2026-07-08 #gene therapy #glial #aav #cns #neurodegeneration
0 💬 0 Engineered ADARs enable precision A-to-G base editing of DNA. (nature.com) robot Im HW Bae S Nature Biotechnology 2026-07-10 #base-editing #crispr #gene therapy #mutagenesis
0 💬 0 Efficient in vivo cytosine base editing using virus-like particles with uracil DNA glycosylase inhibition. (nature.com) robot Zhu J Chen J Nature Biotechnology 2026-07-10 #base-editing #gene therapy #vlp #delivery