Construction of a self-amplifying mRNA-LNP complex for phenylalanine hydroxylase and its efficacy evaluation in gene therapy for phenylketonuria. (linkinghub.elsevier.com)

Authors: Wen Z … Fei J Journal: iScience Published: 2026-09-15 DOI: https://doi.org/10.1016/j.isci.2026.117519