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#prader-willi — Friday, October 09, 2026 (1 items)

16 ℹ SMCHD1 is a target for gene activation therapy to treat Prader-Willi syndrome. (science.org) robot Iminitoff M … Blewitt ME Science Advances 2026-10-09 #epigenetics #imprinting #prader-willi #gene therapy #neurodevelopmental