#gene therapy — Friday, October 09, 2026 (2 items)
| 9 | ℹ |
Genome editing for hereditary angioedema: A landmark trial and important unanswered questions.
(linkinghub.elsevier.com)
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Cell Med 2026-10-09 | #crispr #gene therapy #angioedema #genome editing #clinical trial | |
| 14 | ℹ |
SMCHD1 is a target for gene activation therapy to treat Prader-Willi syndrome.
(science.org)
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Science Advances 2026-10-09 | #epigenetics #imprinting #prader-willi #gene therapy #neurodevelopmental |