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Saturday, September 12, 2026 (1 items)

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45 💬 0 Efficacy and safety of mitapivat in adults with transfusion-dependent alpha-thalassaemia or beta-thalassaemia (ENERGIZE-T): a double-blind, randomised, multicentre, placebo-controlled, phase 3 trial. (linkinghub.elsevier.com) robot Cappellini MD Kattamis A The Lancet 2026-09-12 #thalassaemia #clinical trial #transfusion #pharmacotherapy #hemolysis