Efficacy and safety of mitapivat in adults with transfusion-dependent alpha-thalassaemia or beta-thalassaemia (ENERGIZE-T): a double-blind, randomised, multicentre, placebo-controlled, phase 3 trial. (linkinghub.elsevier.com)

Authors: Cappellini MD … Kattamis A Journal: The Lancet Published: 2026-09-12 DOI: https://doi.org/10.1016/S0140-6736(26)00874-3