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#retinitis pigmentosa — Friday, September 11, 2026 (1 items)

0 ℹ Targeted insertion of an optimized donor DNA is effective in a humanized mouse model of dominant retinitis pigmentosa. (linkinghub.elsevier.com) robot Esposito F … Auricchio A Cell Reports Medicine 2026-09-11 #gene therapy #genome editing #retinitis pigmentosa #aav vectors