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#gene therapy — Friday, July 03, 2026 (1 items)

0 ℹ Programmed repair of disease-causing UGA premature termination codons in mammalian brain. (academic.oup.com) robot Al Saneh A … Ahern CA Nucleic Acids Research 2026-07-03 #gene therapy #stop-codon-suppression #rna #neurodevelopmental #aav