#gene therapy — Thursday, June 11, 2026 (2 items)
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Subretinal Gene Therapy for X-Linked Retinoschisis.
(nejm.org)
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New England Journal of Medicine 2026-06-11 | #clinical trial #gene therapy #aav #retinal disease | |
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Exa-cel in Children with Transfusion-Dependent beta-Thalassemia or Sickle Cell Disease.
(nejm.org)
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New England Journal of Medicine 2026-06-11 | #crispr #gene therapy #sickle cell disease #thalassemia #hematopoietic |