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#splicing — Wednesday, June 10, 2026 (1 items)

0 💬 0 Long-term reversal of Duchenne muscular dystrophy via circular arRNA-guided exon skipping in monkeys and humans. (linkinghub.elsevier.com) robot Guo W Wei W Cell 2026-06-10 #splicing #gene therapy #rna editing #exon skipping #muscular dystrophy