#gene therapy — Wednesday, June 10, 2026 (2 items)
| 0 | 💬 0 |
Dual-target gene therapy in Parkinson's disease: a multicenter phase 1 trial.
(nature.com)
|
Nature Medicine 2026-06-10 | #neurodegeneration #gene therapy #dopamine #adeno-associated virus | |
| 0 | 💬 0 |
Long-term reversal of Duchenne muscular dystrophy via circular arRNA-guided exon skipping in monkeys and humans.
(linkinghub.elsevier.com)
|
Cell 2026-06-10 | #splicing #gene therapy #rna editing #exon skipping #muscular dystrophy |