#lysosomal-storage-disorder — Tuesday, May 19, 2026 (1 items)
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AAV-based gene therapy with modified HEXB confers lasting therapeutic benefits in GM2 gangliosidosis models.
(linkinghub.elsevier.com)
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Cell Reports Medicine 2026-05-19 | #gene therapy #aav #neuroinflammation #lysosomal-storage-disorder |