#knockdown — Wednesday, April 01, 2026 (1 items)
| 0 | 💬 0 |
Antisense oligonucleotide-mediated knockdown therapy in two infants with severe KCNT1 epileptic encephalopathy.
(nature.com)
|
Nature Medicine 2026-04-01 | #antisense #gene therapy #epilepsy #seizures #knockdown |