#antisense — Wednesday, April 01, 2026 (2 items)
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Antisense oligonucleotide-mediated knockdown therapy in two infants with severe KCNT1 epileptic encephalopathy.
(nature.com)
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Nature Medicine 2026-04-01 | #antisense #gene therapy #epilepsy #seizures #knockdown | |
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LRRK2-targeting antisense oligonucleotide in Parkinson's disease: a phase 1 randomized controlled trial.
(nature.com)
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Nature Medicine 2026-04-01 | #clinical trial #pharmacodynamics #neurodegeneration #antisense #neuropathology |