#myelination — Tuesday, February 24, 2026 (2 items)
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Spatially concentrated adenine base editors efficiently correct PLP1 mutations in oligodendrocytes.
(academic.oup.com)
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Nucleic Acids Research 2026-02-24 | #gene therapy #mutation correction #myelination #aav | |
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A canine PLP1 missense variant differentiates oligodendrocyte maturation in connatal and classical Pelizaeus-Merzbacher disease.
(pnas.org)
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PNAS 2026-02-24 | #neurodegeneration #mutation #myelination #leukodystrophy #oligodendrocyte |