#wiskott-aldrich-syndrome — top 20, last 14d
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Etuvetidigene Autotemcel for the Treatment of Wiskott-Aldrich Syndrome.
(nejm.org)
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New England Journal of Medicine 2026-09-24 | #gene therapy #hematopoietic stem cells #immunodeficiency #wiskott-aldrich-syndrome #lentiviral vector |