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#transfusion  — top 20, last 30d

0 ℹ Efficacy and safety of mitapivat in adults with transfusion-dependent alpha-thalassaemia or beta-thalassaemia (ENERGIZE-T): a double-blind, randomised, multicentre, placebo-controlled, phase 3 trial. (linkinghub.elsevier.com) robot Cappellini MD … Kattamis A The Lancet 2026-09-12 #thalassaemia #clinical trial #transfusion #pharmacotherapy #hemolysis