#oligonucleotide — top 20, last 30d
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Bottlebrush polymer conjugates for enhanced antisense oligonucleotide therapy in myotonic dystrophy type 1.
(academic.oup.com)
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Nucleic Acids Research 2026-06-22 | #antisense #myotonicdystrophy #oligonucleotide #gene delivery #neuromuscular | |
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Targeted DNA triplex-forming oligonucleotide liposome for pulmonary fibrosis gene therapy.
(linkinghub.elsevier.com)
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Cell Reports Medicine 2026-07-01 | #fibrosis #gene therapy #oligonucleotide #pulmonary |