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#base-editing — Wednesday, September 30, 2026 (1 items)

1 ℹ Prime editing of human hematopoietic stem cells for correction of GATA2 deficiency. (science.org) robot Wolff JH … Mikkelsen JG Science Translational Medicine 2026-09-30 #genome editing #base-editing #immunodeficiency #hematopoietic #stem-cells