#base-editing — Monday, August 31, 2026 (1 items)
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Mutation-agnostic base editing of the progerin farnesylation site rescues Hutchinson-Gilford progeria syndrome phenotypes in neuromuscular organoids.
(nature.com)
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Nature Communications 2026-08-31 | #base-editing #progeria #organoid #laminopathy #genome editing |