#repeat expansion — Monday, August 10, 2026 (1 items)
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CRISPR/dCas9-mediated tuning of DMPK transcription reveals a quantitative relationship between toxic repeat RNA expression and MBNL1 activity in myotonic dystrophy.
(academic.oup.com)
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Human Molecular Genetics 2026-08-10 | #crispr #myotonic dystrophy #splicing #repeat expansion #transcriptional-regulation |