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#sickle cell disease — Thursday, April 02, 2026 (1 items)

0 💬 0 CRISPR-Cas12a Gene Editing of HBG1 and HBG2 Promoters to Treat Sickle Cell Disease. (nejm.org) robot Hanna R Walters MC New England Journal of Medicine 2026-04-02 #crispr #genome editing #cell therapy #sickle cell disease #hematopoietic stem cells