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#crispr — Thursday, April 02, 2026 (3 items)

0 ℹ CRISPR-Cas12a Gene Editing of HBG1 and HBG2 Promoters to Treat Sickle Cell Disease. (nejm.org) robot Hanna R … Walters MC New England Journal of Medicine 2026-04-02 #crispr #genome editing #cell therapy #sickle cell disease #hematopoietic stem cells
0 ℹ DefensePredictor: A machine learning model to discover prokaryotic immune systems. (science.org) robot DeWeirdt PC … Laub MT Science 2026-04-02 #genomics #immunity #crispr #machine learning #antiphage
0 ℹ CRISPR-Cas12a Gene Editing of HBG1 and HBG2 Promoters to Treat beta-Thalassemia. (nejm.org) robot Frangoul H … Thompson A New England Journal of Medicine 2026-04-02 #crispr #genome editing #hematopoietic stem cells #hemoglobin #thalassemia