#crispr — Thursday, April 02, 2026 (3 items)
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CRISPR-Cas12a Gene Editing of HBG1 and HBG2 Promoters to Treat Sickle Cell Disease.
(nejm.org)
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New England Journal of Medicine 2026-04-02 | #crispr #genome editing #cell therapy #sickle cell disease #hematopoietic stem cells | |
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DefensePredictor: A machine learning model to discover prokaryotic immune systems.
(science.org)
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Science 2026-04-02 | #genomics #immunity #crispr #machine learning #antiphage | |
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CRISPR-Cas12a Gene Editing of HBG1 and HBG2 Promoters to Treat beta-Thalassemia.
(nejm.org)
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New England Journal of Medicine 2026-04-02 | #crispr #genome editing #hematopoietic stem cells #hemoglobin #thalassemia |