#hematopoietic stem cells — Thursday, April 02, 2026 (2 items)
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CRISPR-Cas12a Gene Editing of HBG1 and HBG2 Promoters to Treat Sickle Cell Disease.
(nejm.org)
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New England Journal of Medicine 2026-04-02 | #crispr #sickle cell disease #hematopoietic stem cells #cell therapy #genome editing | |
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CRISPR-Cas12a Gene Editing of HBG1 and HBG2 Promoters to Treat beta-Thalassemia.
(nejm.org)
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New England Journal of Medicine 2026-04-02 | #crispr #thalassemia #hematopoietic stem cells #hemoglobin #genome editing |