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#rna — Wednesday, April 01, 2026 (3 items)

0 ℹ Biallelic variants in the noncoding RNA gene RNU4-2 cause a recessive neurodevelopmental syndrome with distinct white matter changes. (nature.com) robot Rius R … Whiffin N Nature Genetics 2026-04-01 #rna #neurodevelopmental #spliceosome #white matter
0 ℹ Pancreatic-targeted lipid nanoparticles based on organ capsule filtration. (nature.com) robot Lei J … Yu G Nature 2026-04-01 #nanoparticles #immunotherapy #rna #delivery #pancreatic
0 ℹ A structure-based mRNA vaccine for Nipah virus in healthy adults: a phase 1 trial. (nature.com) robot Ploquin A … Dropulic LK Nature Medicine 2026-04-01 #vaccination #clinical trial #rna #immunogenicity #zoonosis