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#blood-brain barrier — Thursday, January 01, 2026 (1 items)

0 ℹ An Intravenous Brain-Penetrant Enzyme Therapy for Mucopolysaccharidosis II. (nejm.org) robot Muenzer J … Ho C New England Journal of Medicine 2026-01-01 #clinical trial #enzyme therapy #lysosomal storage disease #blood-brain barrier